No, we’re not talking about developing drugs for orphans. But for 25 million Americans, according to the NIH, an “Orphan Drug” (one that serves fewer than 200k users and includes diseases such as cystic fibrosis, Lou Gehrig's disease, and Tourette's syndrome, among others) can spell the difference between misery (or worse) and getting through the day. How are traditional vs. orphan drugs...
